OUR
RESEARCH
ON THE WAY
TO MOVE FORWARD
With the resources we get, we want to develop the following strategies: on the one hand, to support worldwide research on our disease and, on the other, to promote the start of research in gene therapy.
··· Video of the research project ···
··· Goals ···
Contribute to the expansion of a data bank (Patient Natural History Study) that collects historical details of people with VHL worldwide.
It is about encouraging potential people for clinical trials and, as far as possible, helping with funding.
Obtain funding to begin research into how to cure VHL syndrome through gene therapy.
··· How? ···
1
A first study of the possibilities that gene therapy can provide for VHL.
The VHL Gene Therapy project will be carried out with the CIMA (Center for Applied Medical Research) research in Navarre.
The CIMA has begun to experiment with research into how to cure monogenic inherited diseases such as VHL through gene therapy,
and about our evil we will begin the research project in the fall of 2019.
2
Supporting ongoing research into the cure for VHL worldwide.
They are doing it for the cure of VHL worldwide data collection on the most significant research and will encourage exchanges and networking between VHL research teams and VHL associations worldwide. To this end, and as a first step, we are compiling a map of the most significant research in the world together with Biodonostia, which will help us to identify and prioritize our collaborative agents.